Genzyme Team Reports Proof-of-concept Data for Expressed RNAi Huntington's Therapy | GenomeWeb

NEW YORK (GenomeWeb) – Researchers from Genzyme this month reported new proof-of-concept data showing that an expressed RNAi approach could be used to both prevent and treat the manifestations of Huntington's disease (HD) in an animal model of the condition.

Though promising, the work is still early stage, cautioned Lisa Stanek, lead author of the study. And while the company is continuing to develop the RNAi-based treatment for HD, clinical studies remain years away, she said.

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