In Dog Study, Scientists Rescue Dystrophin Function with Morpholinos | GenomeWeb

Using morpholinos to induce exon skipping, researchers rescued some dystrophin function in dogs with the canine form of Duchenne muscular dystrophy. Scientists from Children's National Medical Center in Washington, DC, and the National Center of Neurology and Psychiatry in Tokyo restored dystrophin function to about 20 percent of normal levels. "[The] treatment has clearly shown efficacy in a large animal," says lead author Eric Hoffman from Children's, though he adds that the team's Annals of Neurology study was not blinded.

Get the full story with
GenomeWeb Premium

Only $95 for the
first 90 days*

A trial upgrade to GenomeWeb Premium gives you full site access, interest-based email alerts, access to archives, and more. Never miss another important industry story.

Try GenomeWeb Premium now.

Already a GenomeWeb Premium member? Login Now.
Or, See if your institution qualifies for premium access.

*Before your trial expires, we’ll put together a custom quote with your long-term premium options.

Not ready for premium?

Register for Free Content
You can still register for access to our free content.

Biomedical research projects are generating a ton of data that still needs to be analyzed, NPR reports.

Theranos is retiring some of its board members, including Henry Kissinger and George Shultz, Business Insider reports.

The heads of 29 scientific societies and some 2,300 researchers call on President-elect Donald Trump to rely on and support science in two separate letters.

In Science this week: genetically modified flu virus could be key to new live vaccines, and more.