Using morpholinos to induce exon skipping, researchers rescued some dystrophin function in dogs with the canine form of Duchenne muscular dystrophy. Scientists from Children's National Medical Center in Washington, DC, and the National Center of Neurology and Psychiatry in Tokyo restored dystrophin function to about 20 percent of normal levels. "[The] treatment has clearly shown efficacy in a large animal," says lead author Eric Hoffman from Children's, though he adds that the team's Annals of Neurology study was not blinded.

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The New York Times and ProPublica look into the close relationship between a startup and Memorial Sloan Kettering Cancer Center.

Yahoo News reports millions of dollars are being transferred from NIH, CDC, and other programs to pay for the housing of detained undocumented immigrant children.

In Science this week: in vitro generation of human reproductive cells, and more.

Researchers gave a handful of octopuses MDMA to find that they too act more social on the drug, Gizmodo reports.

Nov
05
Sponsored by
Sophia Genetics

With the Next Generation Sequencing (NGS), genomes sequencing has been democratized over the last decades with the detection of genomic alterations, thus replacing Sanger sequencing.