Benitec Announces Positive In Vitro Data from Muscular Dystrophy Program | GenomeWeb

Benitec Biopharma this week announced that it has obtained positive in vitro data from its early-stage program in oculopharyngeal muscular dystrophy.

As a result, Benitec said it and academic collaborators will begin developing a vector that will use expressed RNAi to silence the mutant form of the PABPN1 gene, which causes the condition, and deliver a normal version of the gene.

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The White House has created a list of cuts, including to the NIH, that could be in a budget bill for this year.

The US National Institutes of Health is to allow applicants to cite preprints just as they would any other research paper, ScienceInsider reports.

Two manuscript pages handwritten by Charles Darwin are going on the auction block, according to the Los Angeles Times.

In PNAS this week: tool to track transcriptome-wide binding, evidence of balancing selection on behavior-linked genes, and more.