Arcturus Names TTR Amyloidosis as First Pipeline Program | GenomeWeb

RNAi startup Arcturus Therapeutics this week named transthyretin-mediated amyloidosis as the first indication to be added to its pipeline.

The disease is caused by mutations in the TTR gene, which triggers accumulation of abnormal amyloid proteins in the body. Notably, Alnylam Pharmaceuticals has been developing its own drugs for the disease, with an intravenously delivered one in phase III testing and a subcutaneously administered one in phase II.

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In Nucleic Acids Research this week: personal genome approach to RNA-seq read alignment, hematopoietic Systems Biology Repository, and more.

A man is using DNA evidence to argue that he is the rightful heir to the baronetcy of Stichill, the Guardian reports.

As part of an effort to get a diverse group of people to donate their DNA for research, some blood donors in the San Diego area will get their genomes sequenced, according to KPBS.

The comment period on the Department of Health and Human Services' proposal to alter the Common Rule has been extended.

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