Alnylam Pharmaceuticals this week announced positive clinical results from an ongoing phase II trial of ALN-TTR02, an investigational treatment for TTR-mediated amyloidosis, reporting that the drug was able to knock down levels of the protein that causes the disease by as much as 93 percent.

The gene inhibition was rapid, dose-dependent, and durable, Alnylam said. Additionally, ALN-TTR02 was generally safe and well tolerated in the trial — all of which puts the company on track to move into phase III before the end of the year.

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This webinar will cover recent advances in the use of CRISPR for generating animal models and cell lines.