Alnylam Presents Preclinical Data from Hemophilia, Hemoglobinopathy Programs | GenomeWeb

Alnylam Pharmaceuticals this week presented preclinical data from its hemophilia and bleeding disorder program, showing that its subcutaneously administered drug candidate ALN-AT3 could trigger potent, dose-dependent, durable target knockdown in non-human primates.

The company also reported data indicating that its hemoglobinopathy treatment ALN-TMP had disease-modifying effects in an animal model of B-thalassemia.

The data were presented at the 54th American Society of Hematology annual meeting this week.

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