NEW YORK (GenomeWeb) – Several independent researchers last week shared promising results of their work using the genome-editing tool CRISPR/Cas9 to advance treatments for Duchenne muscular dystrophy.

In a group of three studies published in the Jan. 1 issue of Science, researchers found that after viral delivery into muscle tissue or blood, CRISPR/Cas9 was able to excise disease-associated exons from the dystrophin gene, and improve the symptoms of mice with a rodent version of the disease.

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Sep
12
Sponsored by
PerkinElmer

This webinar will cover recent advances in the use of CRISPR for generating animal models and cell lines.