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NEW YORK (GenomeWeb) – As Phase I testing of its hemophilia therapy ALN-AT3 continues, Alnylam Pharmaceuticals is setting its sights broadly for the program, taking aim at both patients receiving standard medical care as well as those who have become refractory to such treatment, company officials said this week.

"We have a very broad perspective on where this program can go," Alnylam CEO John Maraganore said during a conference call held this week to discuss the firm's third-quarter financial results. "We think it can be very disruptive in the entire hemophilia space."

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Nature News reports that gene therapy approaches are tackling sickle cell disease, but that the cost of treatment is a concern.

The Washington Post reports that a US Senate committee voted this week to approve the nomination of Stephen Hahn to lead the Food and Drug Administration.

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