sickle cell anemia
Fetal Hemoglobin Gene Regulation Study Points to Potential Therapeutic Targets
Regulatory elements revealed in the study could potentially be targeted by base editors to treat conditions like sickle cell disease.
At ESHG, Researchers Present New Noninvasive Prenatal Tests, Disease Recurrence Risk Study
Scientists from the UK and China discussed two new NIPTs that include single-gene disorders and a study to estimate disease recurrence risk in families.
The California startup is about to launch its first product, a noninvasive prenatal screening test for recessive single-gene disorders called Unity.
The former cofounder of Knome believes that the future of precision medicine lies in our ability to program living things to act as medicines.
Horizon Discovery, Rutgers Collaborate to Commercialize CRISPR Base Editing Technology
The partners are planning to integrate the technology into Horizon's research tools and services and to develop it for applications in cell therapeutics.