This Week's Science | GenomeWeb

This Week's Science

In this week’s Science, two Italian research groups reported on promising results from gene therapy clinical trials. In both studies, hematopoietic stem cells were removed from patients, then tranduced with lentiviral vectors encoding therapeutic genes and returned to the patients. For three children with the rare lysosomal storage disorder metachromatic leukodystrophy, which is caused by mutations in the ARSA gene, treatment appears to have halted progression of the disease.

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In Science this week: certain genes repressed during memory formation, analysis of genomes from single neurons, and more.

NASA plans to test whether DNA sequencing studies can be conducted in microgravity.

Congress passes a continuing resolution to keep the US federal government funded through mid-December.

The Human Genome Project was launched 25 years ago, and at Nature, Francis Collins, James Watson, and Eric Green look back at the lessons learned.